The genetic defect–adenosine deaminase (ADA)
deficiency may be cured permanently by
(a) administering adenosine deaminase activators
(b) introducing bone marrow cells producing ADA
into cells at early embryonic stages
(c) enzyme replacement therapy
(d) periodic infusion of genetically engineered
lymphocytes having functional ADA cDNA
deficiency may be cured permanently by
(a) administering adenosine deaminase activators
(b) introducing bone marrow cells producing ADA
into cells at early embryonic stages
(c) enzyme replacement therapy
(d) periodic infusion of genetically engineered
lymphocytes having functional ADA cDNA